Published: Guidance, quality standards and advice
Showing 26 to 28 of 28
| Title | Reference number | Published | Last updated |
|---|---|---|---|
| Eliglustat for treating type 1 Gaucher disease | HST5 | ||
| Migalastat for treating Fabry disease | HST4 | ||
| Eculizumab for treating atypical haemolytic uraemic syndrome | HST1 |