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Onasemnogene abeparvovec for treating presymptomatic spinal muscular atrophy

  • Highly specialised technologies guidance
  • Reference number: HST24
  • Published:  19 April 2023
  • Guidance
  • Tools and resources
  • Information for the public
  • Evidence
  • History

On this page

  1. Expected publication
  2. Final evaluation determination
  3. Invitation to participate
  4. Consultation on suggested remit, draft scope and provisional matrix of consultees and commentators

History

A list of downloadable documents created during development.

Expected publication

  • Register of interests (PDF 288 KB)

    Published:
    19 April 2023
  • Equality Impact Assessment (Guidance development) (PDF 146 KB)

    Published:
    19 April 2023

Final evaluation determination

  • Final evaluation determination

  • Committee papers (PDF 7.54 MB)

    Published:
    16 March 2023
  • Public committee slides (PDF 928 KB)

    Published:
    16 March 2023
  • Final evaluation determination document Equality Impact Assessment (PDF 146 KB)

    Published:
    16 March 2023
  • Final evaluation determination document (PDF 240 KB)

    Published:
    16 March 2023

Invitation to participate

  • Final scope (PDF 172 KB)

    Published:
    09 June 2022
  • NICE's response to comments on the draft scope and provisional stakeholder list (PDF 442 KB)

    Published:
    09 June 2022
  • Equality impact assessment (Scoping) (PDF 126 KB)

    Published:
    09 June 2022
  • Final stakeholder list (PDF 210 KB)

    Published:
    09 June 2022

Consultation on suggested remit, draft scope and provisional matrix of consultees and commentators

  • Draft scope post referral (PDF 189 KB)

    Published:
    22 April 2022
  • Draft matrix post referral (PDF 209 KB)

    Published:
    22 April 2022